Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug - ScienceDirect
REGENXBIO Announces FDA Clearance of IND for Clinical Trial of RGX-202, a Novel Gene Therapy Candidate for Duchenne Muscular Dystrophy · BioBuzz
Clinical Trial Clearance for Gene Therapy Drug - CureDuchenne
CureDuchenne Congratulates Pfizer on Dosing First Patient in Phase III Clinical Trial for Duchenne Muscular Dystrophy - CureDuchenne
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library
Encouraging pipeline for DMD patients - Clinical Trials Arena
Clinical Trials Spotlight - Duchenne Muscular Dystrophy | Office of Research
Genome editing for Duchenne muscular dystrophy: a glimpse of the future? | Gene Therapy