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Promising gene therapy for Duchenne muscular dystrophy
Promising gene therapy for Duchenne muscular dystrophy

Duchenne Muscular Dystrophy - Practical Neurology
Duchenne Muscular Dystrophy - Practical Neurology

Daiichi Sankyo announces Phase 1/2 clinical trial results - Action Duchenne
Daiichi Sankyo announces Phase 1/2 clinical trial results - Action Duchenne

Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a  first-in-class dissociative steroidal anti-inflammatory drug - ScienceDirect
Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug - ScienceDirect

REGENXBIO Announces FDA Clearance of IND for Clinical Trial of RGX-202, a  Novel Gene Therapy Candidate for Duchenne Muscular Dystrophy · BioBuzz
REGENXBIO Announces FDA Clearance of IND for Clinical Trial of RGX-202, a Novel Gene Therapy Candidate for Duchenne Muscular Dystrophy · BioBuzz

Clinical Trial Clearance for Gene Therapy Drug - CureDuchenne
Clinical Trial Clearance for Gene Therapy Drug - CureDuchenne

CureDuchenne Congratulates Pfizer on Dosing First Patient in Phase III Clinical  Trial for Duchenne Muscular Dystrophy - CureDuchenne
CureDuchenne Congratulates Pfizer on Dosing First Patient in Phase III Clinical Trial for Duchenne Muscular Dystrophy - CureDuchenne

Peak functional ability and age at loss of ambulation in Duchenne muscular  dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology -  Wiley Online Library
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library

Encouraging pipeline for DMD patients - Clinical Trials Arena
Encouraging pipeline for DMD patients - Clinical Trials Arena

Clinical Trials Spotlight - Duchenne Muscular Dystrophy | Office of Research
Clinical Trials Spotlight - Duchenne Muscular Dystrophy | Office of Research

Genome editing for Duchenne muscular dystrophy: a glimpse of the future? |  Gene Therapy
Genome editing for Duchenne muscular dystrophy: a glimpse of the future? | Gene Therapy

Duchenne Muscular Dystrophy Disease - Global Clinical Trials Review, H2,  2020
Duchenne Muscular Dystrophy Disease - Global Clinical Trials Review, H2, 2020

About Clinical Trials – Defeat Duchenne Canada
About Clinical Trials – Defeat Duchenne Canada

SJD Barcelona Children's Hospital in a trial on Duchenne muscular dystrophy
SJD Barcelona Children's Hospital in a trial on Duchenne muscular dystrophy

Global Duchenne Muscular Dystrophy Clinical Trial Pipeline Highlights - 2021
Global Duchenne Muscular Dystrophy Clinical Trial Pipeline Highlights - 2021

Participants Sought for Clinical Trial to Test Vamorolone in DMD - Muscular  Dystrophy Association
Participants Sought for Clinical Trial to Test Vamorolone in DMD - Muscular Dystrophy Association

Clinical trial of gene therapy for Duchenne muscular dystrophy underway at  University of Florida Health | UF Health, University of Florida Health
Clinical trial of gene therapy for Duchenne muscular dystrophy underway at University of Florida Health | UF Health, University of Florida Health

Research and Clinical Trials
Research and Clinical Trials

VISION-DMD – Designed to ensure a timely & cost-effective drug development  for Duchenne muscular dystrophy
VISION-DMD – Designed to ensure a timely & cost-effective drug development for Duchenne muscular dystrophy

Duchenne Drug Development Pipeline - Parent Project Muscular Dystrophy
Duchenne Drug Development Pipeline - Parent Project Muscular Dystrophy

First BMD Patients Dosed in Phase 1 Trial of Oral Therapy EDG-5506
First BMD Patients Dosed in Phase 1 Trial of Oral Therapy EDG-5506

Sarepta issues clinical trials update - Action Duchenne
Sarepta issues clinical trials update - Action Duchenne

Unmet needs in Duchenne muscular dystrophy will be partially met by the  pipeline, says GlobalData - GlobalData
Unmet needs in Duchenne muscular dystrophy will be partially met by the pipeline, says GlobalData - GlobalData

Wave Life Sciences Announces Positive Results of Phase 1 Trial of  WVE-210201 for Duchenne Muscular Dystrophy - Muscular Dystrophy Association
Wave Life Sciences Announces Positive Results of Phase 1 Trial of WVE-210201 for Duchenne Muscular Dystrophy - Muscular Dystrophy Association

Measurements Used in Clinical Trials for Duchenne Muscular Dystrophy – an  Overview | Sarepta Therapeutics
Measurements Used in Clinical Trials for Duchenne Muscular Dystrophy – an Overview | Sarepta Therapeutics

Top 10 Duchenne Muscular Dystrophy Clinical Trials [2022 Studies] | Power
Top 10 Duchenne Muscular Dystrophy Clinical Trials [2022 Studies] | Power

Ongoing clinical trials 1 and approval status of therapeutic approaches...  | Download Table
Ongoing clinical trials 1 and approval status of therapeutic approaches... | Download Table

Duchenne Muscular Dystrophy - Global Clinical Trials Review, H2, 2021
Duchenne Muscular Dystrophy - Global Clinical Trials Review, H2, 2021